A Generative and Causal Pharmacokinetic Model for Factor VIII in Hemophilia
CLINICAL PHARMACOLOGY & THERAPEUTICS | VOLUME 0 NUMBER 0 | Month 2024 doi:10.1002/cpt.3203
PBPK modeling of recombinant factor IX Fc fusion protein
CPT Pharmacometrics Syst Pharmacol. 2024;13:1630–1640 Lees hier
PhD defense Michael Cloesmeijer
On the 18th of December 2024 Michael Cloesmeijer, PhD WP06, defended his thesis "The dynamics of pharmacometrics to personalize the treatment of inborn bleeding disorders". If you missed the PhD defence you can watch it now (this video is in Dutch) by clickin HERE. To read the thesis you [...]
PhD defence Shannon van Hoorn
On the 27th of November 2024 Shannon van Hoorn, PhD WP05, defended here thesis "Value-Based Healthcare In Inherited Bleeding Disorders". If you missed the PhD defence you can watch it now (this video is in Dutch): https://www.youtube.com/live/Wtni27KZacA To read the thesis you can scroll down to the pfd below. [...]
SYMPHONY @ SOCIETY MEDICAL DECISION MAKING CONFERENCE
From October 27–30, 2024, SYMPHONY PhD candidate Diaz Prameyllawati attended the Society for Medical Decision Making (SMDM) conference in Boston, presenting her research on the care organization and costs of delivering gene therapy for hemophilia in the Netherlands. During a two-hour poster session at the SMDM conference, Diaz engaged in [...]
Platelet proteomics profiling in sitosterolemia suggests
Blood Advances 28 MAY 2024 • VOLUME 8, NUMBER 10
Joint status of patients with nonservere hemophilia A
J Thromb Haemost. 2022;20:1126–1137 DOI: 10.1111/jth.15676
Blood coagulation and beyond
Thromb Haemost 2023; 123:808-839 Het article kan HIER gelezen worden
Hoe AI de Zorg voor Zeldzame Aandoeningen Transformeert
Binnen ons onderzoeksconsortium zetten we AI in om de zorg voor mensen met zeldzame aandoeningen te verbeteren. Wereldwijd leven miljoenen mensen met een zeldzame aandoening, vaak zonder effectieve behandelingen of een tijdige diagnose. Dit vraagt om innovatieve oplossingen – en hier komt AI om de hoek kijken. Met behulp van [...]
SYMPHONY on tour: Interview with Renske ten Ham
SYMPHONY on tour: Interview with Dr. Renske ten Ham (NWO VENI laureate 2024) Dr. Renske ten Ham is an Assistant Professor at the UMC Utrecht and specializes in health economics and health technology assessment (HTA) of regenerative medicines. She is one of the supervisors of Work package 8, which focuses [...]